DOI:
10.1055/s-00000031
Klinische Monatsblätter für Augenheilkunde
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References
Burnight ER, Wiley LA, Drack AV. et al.
CEP290 gene transfer rescues Leber congenital amaurosis cellular phenotype.
Gene Ther 2014;
21: 662-672
doi:10.1038/gt.2014.39
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