Study Design of STR1VE-EU, a Phase 3 Trial of AVXS-101 Gene-Replacement Therapy (GRT) in Patients With Spinal Muscular Atrophy Type 1 (SMA1) in Europe - Muntoni, Francesco; Baranello, Giovanni; Bruno, Claudio; Corti, Stefania; Masson, Riccardo; Straub, Volker; Vita, Giuseppe; Ernst, Uwe; Kernbauer, Elaine; Williamson, Susan; Ouyang, Haojun; Feltner, Douglas E.; Meriggioli, Matthew; Lavrov, Arseniy; L’Italien, James; Sproule, Douglas M.; Mercuri, Eugenio (Neuropediatrics, 2019)