DOI: 10.1055/s-00000140

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References

Haas M, Vlcek V, Balabanov P. et al.
European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene.

Neuromuscul Disord 2015;
1: 5-13
doi:10.1016/j.nmd.2014.11.011

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