DOI: 10.1055/s-00035024

Thrombosis and Haemostasis

References

Yoneyama K, Schmitt C, Kotani N. et al.
A pharmacometric approach to substitute for a conventional dose-finding study in rare diseases: example of phase III dose selection for emicizumab in hemophilia A.

Clin Pharmacokinet 2018;
57 (09) 1123-1134

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