DOI: 10.1055/s-00000041

Neuropediatrics

References

Cortina-Borja M, Te Vruchte D, Mengel E. et al.
Annual severity increment score as a tool for stratifying patients with Niemann-Pick disease type C and for recruitment to clinical trials.

Orphanet J Rare Dis 2018;
13 (01) 143

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