DOI: 10.1055/s-00000041

Neuropediatrics

References

Stolte B, Totzeck A, Kizina K. et al.
Feasibility and safety of intrathecal treatment with nusinersen in adult patients with spinal muscular atrophy.

Ther Adv Neurol Disorder 2018;
11: 1756286418803246

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