DOI:
10.1055/s-00000041
Neuropediatrics
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References
Strauss KA, Carson VJ, Brigatti KW. et al.
Preliminary safety and tolerability of a novel subcutaneous intrathecal catheter system for repeated outpatient dosing of nusinersen to children and adults with spinal muscular atrophy.
J Pediatr Orthop 2018;
38 (10) e610-e617
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