DOI: 10.1055/s-00000041

Neuropediatrics

References

Kishnani PS, Hwu WL, Mandel H, Nicolino M, Yong F, Corzo D. ; Infantile-Onset Pompe Disease Natural History Study Group.
A retrospective, multinational, multicenter study on the natural history of infantile-onset Pompe disease.

J Pediatr 2006;
148 (05) 671-676

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