DOI: 10.1055/s-00029022

Journal of Pediatric Biochemistry

References

Trefz FK, Burton BK, Longo N , et al; Sapropterin Study Group.
Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study.

J Pediatr 2009;
154 (5) 700-707

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