DOI: 10.1055/s-00000041

Neuropediatrics

References

Kurai T, Hisayasu S, Kitagawa R. et al.
AAV1 mediated co-expression of formylglycine-generating enzyme and arylsulfatase a efficiently corrects sulfatide storage in a mouse model of metachromatic leukodystrophy. 
Mol Ther 2007; 15: 38-43  

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