DOI: 10.1055/s-00000031

Klinische Monatsblätter für Augenheilkunde

References

Han Z, Conley SM, Makkia RS. et al.
DNA nanoparticle-mediated ABCA4 delivery rescues Stargardt dystrophy in mice.

J Clin Invest 2012;
122: 3221-3226
doi:10.1172/JCI64833

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