DOI: 10.1055/s-00000032

Klinische Neurophysiologie

References

Adams D, Gonzalez-Duarte A, O'Riordan WD. et al.
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis.

N Engl J Med 2018;
379: 11-21

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